Use of Nusinersen in type 1 Spinal Muscular Atrophy. Literature Review . Research, Society and Development, [S. l.], v. 11, n. 4, p. e33811427297, 2022. DOI: 10.33448/rsd-v11i4.27297. Disponível em: https://rsdjournal.org/rsd/article/view/27297. Acesso em: 5 dec. 2025.